FDA Approves 2 Gene Therapies for Sickle Cell Disease. One is the first to use the editing tool CRISPR
Regulators on Friday approved two gene therapies for sickle cell disease that doctors hope can cure the painful, inherited blood disorder that mainly affects black people in the US. The Food and Drug Administration said the one-time treatments can be used for patients 12 years and older with severe forms of the disease. One, made … Read more