The two children of Gautam Dongre in India and the son of Pascazia Mazeze in Tanzania live with an inherited blood disease that turns blood cells into instruments of pain. With new gene therapies promising a cure for their sickle cell disease, Dongre says he is “praying for the treatment to come to us.” But … Read more
The two children of Gautam Dongre in India and the son of Pascazia Mazeze in Tanzania live with an inherited blood disease that turns blood cells into instruments of pain. With new gene therapies promising a cure for their sickle cell disease, Dongre says he is “praying for the treatment to come to us.” But … Read more
Regulators on Friday approved two gene therapies for sickle cell disease that doctors hope can cure the painful, inherited blood disorder that mainly affects black people in the US. The Food and Drug Administration said the one-time treatments can be used for patients 12 years and older with severe forms of the disease. One, made … Read more