Why genetically modified fish are bred to combat rare childhood diseases

Scientists have genetically engineered a new breed of zebrafish with transparent skin to accurately observe its internal organs – Richard White/Children’s Hospital Boston At the heart of Doha’s Education City, a sprawling, sun-drenched campus of technology companies and universities, lies a healthcare facility that Qatar hopes will become a beacon of personalized medicine in the … Read more

Promising new gene therapies for sickle cell disease are out of reach in countries where they are needed most

The two children of Gautam Dongre in India and the son of Pascazia Mazeze in Tanzania live with an inherited blood disease that turns blood cells into instruments of pain. With new gene therapies promising a cure for their sickle cell disease, Dongre says he is “praying for the treatment to come to us.” But … Read more

Promising new gene therapies for sickle cell disease are out of reach in countries where they are needed most

The two children of Gautam Dongre in India and the son of Pascazia Mazeze in Tanzania live with an inherited blood disease that turns blood cells into instruments of pain. With new gene therapies promising a cure for their sickle cell disease, Dongre says he is “praying for the treatment to come to us.” But … Read more

FDA Approves 2 Gene Therapies for Sickle Cell Disease. One is the first to use the editing tool CRISPR

Regulators on Friday approved two gene therapies for sickle cell disease that doctors hope can cure the painful, inherited blood disorder that mainly affects black people in the US. The Food and Drug Administration said the one-time treatments can be used for patients 12 years and older with severe forms of the disease. One, made … Read more